orphan drug

基本解釋

Objective: To introduce American Orphan Drug System.
目的：介紹美國(guó)罕見(jiàn)病藥物制度。
A drug is eligible for orphan drug designation if it is intended to treat a disease or condition that affects less than 200,000 people in the United States.
當(dāng)一種疾病影響小于20萬(wàn)美國(guó)人時(shí)，治療該疾病的藥品被指定為稀少藥品。
Orphan drug designation is available for drugs already approved for another disease or condition or for experimental drugs that have not been previously approved.
已經(jīng)被批準(zhǔn)用于其它疾病治療的藥物或者是尚處于試驗(yàn)階段未被批準(zhǔn)的藥物都可以通過(guò)孤兒藥物申報(bào)程序進(jìn)行。

Without the Orphan Drug Act, there would probably be no Biogen Idec, no Genzyme, Alexion Pharmaceuticals.
FORBES: How The Odd Couple's Jack Klugman Helped Create The Biotech Industry
One idea is to create an incentive for drugmakers comparable to that in the Orphan Drug Act.
FORBES: Magazine Article
AZT, began as an orphan drug for what was then an obscure disease of the immune system.
ECONOMIST: Rare diseases: Safety in numbers